On Friday, Shu Yilai, a professor and practicing surgeon at Fudan University in Shanghai, shared results of the trial, in which young patients received injections of...
Shu also thinks the treatment can be made more potent. But already, he says, the children’s hearing improved, on average, from not hearing anything under 95...
Ilya Sutskever, OpenAI’s cofounder and chief scientist, is no longer focusing on building the next generation of his company’s flagship generative AI models. Instead his new...
For the chicken study, the team made changes to a protein gene in the birds’ sperm and eggs. This protein, called ANP32A, helps flu viruses attack...
The news: Last week, the US Food and Drug Administration approved sales of the first gene therapy that is directly applied to the body—as well as...
“I think it is really exciting, but I do worry about how durable the treatment is,” says Denitsa Milanova, founder of a Boston startup, Marble Therapeutics,...
Follistatin is a glycoprotein encoded by the FST gene. To Minicircle, its most interesting property is that it suppresses myostatin, a protein that inhibits muscle growth....
Last year, biotech startup Minicircle started recruiting participants for a clinical trial of gene therapy. But several details made it unusual. For one, it instructed would-be...
That vision is not far off, researchers say. Advances in gene editing, and CRISPR technology in particular, may soon make it possible. In the early days,...
We know the basics of healthy living by now. A balanced diet, regular exercise, and stress reduction can help us avoid heart disease—the world’s biggest killer....